New scientific publication
Spinal muscular atrophy (SMA) is characterized by the breakdown of motor neurons in the midbrain, medulla oblongata and spinal cord. In this study, we use registry data to show how survival has improved after the introduction of the first drug for children diagnosed with SMA, please read:
https://www.ejpn-journal.com/article/S1090-3798(22)00116-7/fulltext#%20